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gene-therapy: Archive

Zacks Equity Research

VERV Stock Soars on Superior Efficacy in Phase I Cholesterol Study

Verve Therapeutics stock rises on demonstrating superior LDL-C lowering ability in a phase Ib study of VERVE-102 in patients with HeFH and/or CAD.

LLYPositive Net Change BAYRYPositive Net Change ADMANegative Net Change VERVPositive Net Change

Zacks Equity Research

PCRX Doses First Patient in Phase II PCRX-201 Gene Therapy Study

Pacira doses the first patient in the phase II ASCEND study of PCRX-201 gene therapy for OA of the knee.

DVAXPositive Net Change BAYRYPositive Net Change PCRXNegative Net Change CORTPositive Net Change

Zacks Equity Research

SRPT Stock Down After EMA Places Clinical Hold on DMD Gene Therapy

The EMA pauses all clinical studies of Sarepta and Roche's Elevidys following the reported death of a treated patient

RHHBYPositive Net Change SRPTNegative Net Change ANIPNegative Net Change CTMXPositive Net Change

Sundeep Ganoria

Biotech Stocks Fall After Top FDA Official Quits Over Clash With RFK Jr.

The decline in biotech stocks comes after FDA official Peter Marks' resignation, citing irreconcilable differences with the new HHS Secretary.

MRNANegative Net Change NVAXNegative Net Change SRPTNegative Net Change CRSPPositive Net Change PCVXNo Net Change

Urmimala Biswas

3 Stocks to Watch in the Evolving Cell-Based Ophthalmic Therapy Space

ALC, GKOS and REGN are well-positioned to benefit from the evolving space of cell-based ophthalmic therapy.

REGNPositive Net Change ALCPositive Net Change GKOSPositive Net Change

Ekta Bagri

Promising Genomics & Synthetic Biology Stocks to Consider in 2025

Investors interested in the Genomics and Synthetic Biology theme should consider these stocks: Twist Bioscience Corporation, Wave Life Sciences, and CRISPR Therapeutics AG.

ILMNPositive Net Change BEAMNegative Net Change WVEPositive Net Change NTLAPositive Net Change CRSPPositive Net Change TWSTPositive Net Change

Sundeep Ganoria

How to Play SRPT Stock After Patient Death Post DMD Therapy Infusion

We advise investors with a long-term horizon to remain invested in Sarepta stock, given its encouraging commercial portfolio and robust pipeline potential.

RHHBYPositive Net Change SRPTNegative Net Change PTCTPositive Net Change ARWRPositive Net Change

Zacks Equity Research

Novartis Reports Updated Positive Data From Phase III SMA Program

NVS reports new safety and efficacy data from the phase III program for its investigational OAV101 IT gene therapy for SMA patients.

NVSPositive Net Change RHHBYPositive Net Change DVAXPositive Net Change GILDNegative Net Change

Zacks Equity Research

SRPT Nosedives 27% on Patient Death Following DMD Therapy Infusion

Despite the reported death, Sarepta maintains that its gene therapy has a favorable 'benefit-risk profile.'

RHHBYPositive Net Change SRPTNegative Net Change ANIPNegative Net Change CTMXPositive Net Change

Sundeep Ganoria

CRISPR Therapeutics Stock Trades Near 52-Week Low: Time to Buy or Sell?

The fall in CRSP stock can be attributed to a lack of pipeline updates. Despite securing approval for its first marketed product in early 2024, it is yet to record product sales.

VRTXPositive Net Change BEAMNegative Net Change NTLAPositive Net Change CRSPPositive Net Change

Zacks Equity Research

SLDB Stock Rallies 60% in a Month: Here's What You Should Know

Solid Biosciences stock soars 60% in a month after the company announced positive initial data from its phase I/II DMD study of SGT-003.

BIIBPositive Net Change RHHBYPositive Net Change SRPTNegative Net Change SLDBPositive Net Change

Zacks Equity Research

Editas Q4 Loss Wider Than Expected, Revenues Fall Y/Y, Stock Down

EDIT stock is down following the announcement of dismal fourth-quarter 2024 results as both earnings and revenues miss estimates.

BMRNPositive Net Change GILDNegative Net Change VRTXPositive Net Change EDITPositive Net Change