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gene-therapy: Archive

Zacks Equity Research

REGENXBIO (RGNX) Soars 15% on Interim Data From DMD Study

Data from an early-stage study shows that treatment with REGENXBIO's (RGNX) investigational Duchenne therapy RGX-202 demonstrates early evidence of strength and motor function improvement.

SRPTNegative Net Change ADMAPositive Net Change RGNXNegative Net Change SLDBNegative Net Change

Zacks Equity Research

Sarepta (SRPT) Q4 Earnings Beat Estimates, Revenues Up Y/Y

Sarepta's (SRPT) Q4 earnings and sales beat estimates on the back of strong sales for recently-approved DMD gene therapy Elevidys.

RHHBYPositive Net Change ACETNegative Net Change SRPTNegative Net Change PBYIPositive Net Change

Zacks Equity Research

Editas (EDIT) Q4 Earnings & Revenues Top Estimates, Stock Up

Editas (EDIT) reports better-than-expected fourth-quarter 2023 results as both earnings and revenues beat estimates, driven by collaboration revenues received from Vertex. The stock gains 25%.

VRTXPositive Net Change ACETNegative Net Change EDITNegative Net Change AKROPositive Net Change

Zacks Equity Research

BioMarin (BMRN) Posts Q4 Earnings Beat, Upbeat Voxzogo Sales

BioMarin (BMRN) reports encouraging fourth-quarter results, with earnings and sales beating estimates. The rapid uptake of Voxzogo boosts revenues.

SNYPositive Net Change BMRNNegative Net Change ACETNegative Net Change PBYIPositive Net Change

Zacks Equity Research

CRISPR (CRSP) Q4 Earnings Top on Collaboration Revenues, Stock Up

CRISPR (CRSP) gains on encouraging fourth-quarter 2023 results, beating both earnings and revenue estimates on the back of collaboration revenues received from Vertex.

VRTXPositive Net Change PBYIPositive Net Change ADMAPositive Net Change CRSPNegative Net Change

Zacks Equity Research

Sarepta (SRPT) to Report Q4 Earnings: Will It Beat Estimates?

Investors' focus will likely be on Sarepta's (SRPT) product sales of its recently-approved DMD gene therapy when it reports fourth-quarter earnings.

RHHBYPositive Net Change SRPTNegative Net Change ARQTNegative Net Change CGEMNegative Net Change

Zacks Equity Research

Sarepta's (SRPT) DMD Drug sBLA Gets FDA's Priority Tag, Stock Up

Sarepta (SRPT) announces the FDA's acceptance of its efficacy supplement to the Elevidys BLA, seeking to expand the treatment label for its DMD drug. The stock gains 8%.

RHHBYPositive Net Change SRPTNegative Net Change ADMAPositive Net Change IMCRPositive Net Change

Zacks Equity Research

REGENXBIO's (RGNX) Hunter Syndrome Study Meets Goal, Stock Up

REGENXBIO (RGNX) gains 12% on positive top-line results from the phase I/II/III study of its investigational one-time gene therapy candidate, RGX-121, to treat pediatric patients with Hunter syndrome.

PBYIPositive Net Change RGNXNegative Net Change IMCRPositive Net Change

Zacks Equity Research

Vertex's (VRTX) Non-Opioid Pain Drug Meets Primary Goal

Three late-stage studies data show that Vertex's (VRTX) experimental non-opioid drug reduced pain across a 48-hour period. Based on this data, VRTX intends to submit an FDA filing by mid-2024.

VRTXPositive Net Change SRPTNegative Net Change AVXLNegative Net Change CRSPNegative Net Change