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gene-therapy: Archive

Zacks Equity Research

Ultragenyx's Gene Therapy for Sanfilippo Syndrome Wins EMA Validation

RARE's gene therapy for Sanfilippo syndrome wins EMA validation, advancing the treatment toward formal review in Europe.

RARENegative Net Change ALDXPositive Net Change ACIUPositive Net Change PGENPositive Net Change

Zacks Equity Research

RARE Stock Up 13% on FDA Approval of Sanfilippo Syndrome Gene Therapy

Ultragenyx jumps 13% after FDA approval of Fayuvi, the first approved treatment for Sanfilippo syndrome Type A, backed by durable clinical data.

RARENegative Net Change ALDXPositive Net Change ACIUPositive Net Change PGENPositive Net Change

Ekta Bagri

3 Promising Genomics Stocks in the Spotlight in 2026

Genomics is reshaping healthcare, with WGS, NEO and NTLA advancing diagnostics and precision medicine.

NEOPositive Net Change NTLAPositive Net Change WGSNegative Net Change ILMNPositive Net Change BEAMPositive Net Change CRSPPositive Net Change