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gene-therapy: Archive

Zacks Equity Research

Sarepta Q4 Earnings Lag Estimates, Revenues Gain on Gene Therapy Sales

SRPT reports mixed fourth-quarter 2024 results. It closes the multi-billion-dollar deal with Arrowhead and adds four new clinical programs to its pipeline.

RHHBYPositive Net Change SRPTNegative Net Change ARWRPositive Net Change

Zacks Equity Research

CRISPR Therapeutics Q4 Earnings and Revenues Surpass Estimates

CRSP reports encouraging fourth-quarter results. The commercial launch of the first CRISPR-based gene therapy, Casgevy, is progressing well.

ALNYNegative Net Change BMRNPositive Net Change VRTXPositive Net Change CRSPPositive Net Change

Zacks Equity Research

RARE Reports New Upbeat Data From Sanfilippo Syndrome Drug Study

Ultragenyx announces new safety and efficacy data from its pivotal study of its investigational candidate, UX111, for patients with Sanfilippo syndrome type A.

ALNYNegative Net Change BMRNPositive Net Change RAREPositive Net Change CSTLNegative Net Change

Sundeep Ganoria

SRPT Stock Rises 23% in a Year: Time to Buy, Hold or Sell?

The upside in Sarepta's share price can be attributed to the encouraging sales performance of its DMD gene therapy, which has demonstrated blockbuster potential.

RHHBYPositive Net Change SRPTNegative Net Change ARWRPositive Net Change

Zacks Equity Research

RARE Submits BLA to the FDA for Sanfilippo Syndrome Gene Therapy

Ultragenyx submits a BLA to the FDA seeking the accelerated approval of UX111 for patients with Sanfilippo syndrome type A in the United States.

RAREPositive Net Change CTMXPositive Net Change SPROPositive Net Change CSTLNegative Net Change