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gene-therapy: Archive

Zacks Equity Research

Insmed's Q1 Loss Wider Than Expected, Sales Match Estimates

INSM posts wider-than-expected loss in the first quarter. It reiterates the 2025 sales outlook for Arikayce in the range of $405-$425 million.

BEAMNegative Net Change INSMNegative Net Change ADPTPositive Net Change

Zacks Equity Research

SRPT Q1 Earnings Miss, Sales Beat, Stock Slides 21% on '25 View Cut

SRPT reports mixed first-quarter 2025 results. The stock plunges after the company significantly lowers its 2025 sales guidance.

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Zacks Equity Research

DTIL Gets FDA's Fast Track Tag for Hepatitis B Gene Therapy, Stock Up

Precision BioSciences stock soars 24% as the FDA grants the Fast Track designation to its PBGENE-HBV gene therapy for potentially curing chronic hepatitis B.

DVAXPositive Net Change BAYRYNegative Net Change ADMANegative Net Change DTILNegative Net Change

Zacks Equity Research

SRPT Provides Pipeline Updates on Rare Muscular Disorder Therapies

Following positive FDA feedback, Sarepta advances a fourth LGMD program to clinical development.

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Zacks Equity Research

VERV Stock Soars on Superior Efficacy in Phase I Cholesterol Study

Verve Therapeutics stock rises on demonstrating superior LDL-C lowering ability in a phase Ib study of VERVE-102 in patients with HeFH and/or CAD.

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Zacks Equity Research

PCRX Doses First Patient in Phase II PCRX-201 Gene Therapy Study

Pacira doses the first patient in the phase II ASCEND study of PCRX-201 gene therapy for OA of the knee.

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Zacks Equity Research

SRPT Stock Down After EMA Places Clinical Hold on DMD Gene Therapy

The EMA pauses all clinical studies of Sarepta and Roche's Elevidys following the reported death of a treated patient

RHHBYNegative Net Change SRPTNegative Net Change ANIPPositive Net Change CTMXNegative Net Change

Sundeep Ganoria

Biotech Stocks Fall After Top FDA Official Quits Over Clash With RFK Jr.

The decline in biotech stocks comes after FDA official Peter Marks' resignation, citing irreconcilable differences with the new HHS Secretary.

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Urmimala Biswas

3 Stocks to Watch in the Evolving Cell-Based Ophthalmic Therapy Space

ALC, GKOS and REGN are well-positioned to benefit from the evolving space of cell-based ophthalmic therapy.

REGNNegative Net Change ALCNegative Net Change GKOSPositive Net Change

Ekta Bagri

Promising Genomics & Synthetic Biology Stocks to Consider in 2025

Investors interested in the Genomics and Synthetic Biology theme should consider these stocks: Twist Bioscience Corporation, Wave Life Sciences, and CRISPR Therapeutics AG.

ILMNNegative Net Change BEAMNegative Net Change WVENegative Net Change NTLANegative Net Change CRSPPositive Net Change TWSTNegative Net Change